CRISPR/Cas9-generated mouse model of Duchenne muscular dystrophy recapitulating a newly identified large 430 kb deletion in the human DMD gene TV Egorova, ED Zotova, DA Reshetov, AV Polikarpova, SG Vassilieva, ... Disease Models & Mechanisms 12 (4), dmm037655, 2019 | 44 | 2019 |
A novel hairpin-like antimicrobial peptide from barnyard grass (Echinochloa crusgalli L.) seeds: structure–functional and molecular-genetics characterization DY Ryazantsev, EA Rogozhin, TV Dimitrieva, PE Drobyazina, ... Biochimie 99, 63-70, 2014 | 38 | 2014 |
Muscle-specific promoters for gene therapy VV Skopenkova, TV Egorova, MV Bardina Acta Naturae 13 (1), 47, 2021 | 27 | 2021 |
Therapeutic potential of highly functional codon-optimized microutrophin for muscle-specific expression AV Starikova, VV Skopenkova, AV Polikarpova, DA Reshetov, ... Scientific Reports 12 (1), 848, 2022 | 17 | 2022 |
PCR-based analytical methods for quantification and quality control of recombinant adeno-associated viral vector preparations AA Shmidt, TV Egorova Pharmaceuticals 15 (1), 23, 2021 | 17 | 2021 |
Current advances in gene therapy of mitochondrial diseases VO Soldatov, MV Kubekina, MY Skorkina, AE Belykh, TV Egorova, ... Journal of translational medicine 20 (1), 562, 2022 | 15 | 2022 |
In vitro assay for the efficacy assessment of AAV vectors expressing microdystrophin KA Danilov, SG Vassilieva, AV Polikarpova, AV Starikova, AA Shmidt, ... Experimental Cell Research 392 (2), 112033, 2020 | 11 | 2020 |
Модификация метода анализа результатов редактирования генома с помощью системы CRISPR/Cas9 на предимплантационных эмбрионах мыши ТВ Димитриева, ДА Решетов, ВЕ Жерновков, ДВ Влодавец, ЕД Зотова, ... Вестник Российского государственного медицинского университета, 16-22, 2016 | 8 | 2016 |
Adeno-associated viruses for modeling neurological diseases in animals: achievements and prospects E Lunev, A Karan, T Egorova, M Bardina Biomedicines 10 (5), 1140, 2022 | 7 | 2022 |
AAV infection of bovine embryos: Novel, simple and effective tool for genome editing AS Krivonogova, AV Bruter, VA Makutina, YD Okulova, LA Ilchuk, ... Theriogenology 193, 77-86, 2022 | 6 | 2022 |
Duchenne muscular dystrophy animal models TV Egorova, II Galkin, YV Ivanova, AV Polikarpova Preclinical Animal Modeling in Medicine, 107, 2022 | 5 | 2022 |
Анализ фенотипических проявлений делеций в гене дистрофина в контексте эффективности пропуска экзон0в как метода терапии наследственных дистрофинопатий ЕД Зотова, ДА Решетов, ВЕ Жерновков, ДВ Влодавец, ТВ Димитриева, ... Вестник Российского государственного медицинского университета, 23-29, 2016 | 5 | 2016 |
Modification of the method for analysis of genome editing results using CRISPR/Cas9 system on preimplantation mouse embryos TV Dimitrieva, DA Reshetov, VE Zhernovkov, DV Vlodavets, ED Zotova, ... Bulletin of Russian State Medical University, 15-20, 2016 | 5 | 2016 |
CRISPR/Cas9-generated mouse model with humanizing single-base substitution in the Gnao1 for safety studies of RNA therapeutics AV Polikarpova, TV Egorova, EA Lunev, AA Tsitrina, SG Vassilieva, ... Frontiers in Genome Editing 5, 1034720, 2023 | 4 | 2023 |
CRISPR-Cas9 correction in the DMD mouse model is accompanied by upregulation of Dp71f protein TV Egorova, AV Polikarpova, SG Vassilieva, MA Dzhenkova, ... Molecular Therapy-Methods & Clinical Development 30, 161-180, 2023 | 3 | 2023 |
DMD TREATMENT: ANIMAL MODELS: P. 203Exons 6 and 7 skipping test on new murine model of Duchenne muscular dystrophy T Egorova, D Reshetov, A Polikarpova, S Vassilieva, D Vlodavets, ... Neuromuscular Disorders 28, S94, 2018 | 3 | 2018 |
In-frame deletion of dystrophin exons 8–50 results in DMD phenotype TV Egorova, II Galkin, OA Velyaev, SG Vassilieva, IM Savchenko, ... International Journal of Molecular Sciences 24 (11), 9117, 2023 | 2 | 2023 |
Genetically modified animal models of hereditary diseases for testing of gene-directed therapy AV Polikarpova, TV Egorova, MV Bardina Research Results in Pharmacology 8 (2), 11-26, 2022 | 1 | 2022 |
RNAi-based gene therapy approach for GNAO1-related neurodevelopmental disorder MV Bardina, AV Polikarpova, EM Loseva, SG Vassilieva, TV Egorova Human Gene Therapy 30 (11), P270, 2019 | 1 | 2019 |
RNA Interference Effectors Selectively Silence the Pathogenic Variant GNAO1 c.607 G > A In Vitro NV Klementieva, EA Lunev, AA Shmidt, EM Loseva, IM Savchenko, ... nucleic acid therapeutics 34 (2), 90-99, 2024 | | 2024 |