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Developing Epigenetic Therapies for Haploinsufficiency NR Punjya UC Davis, 2023 | | 2023 |
Rescuing the Haploinsufficiency in 22Q11. 2 Deletion Syndrome NR Punjya MOLECULAR THERAPY 29 (4), 190-190, 2021 | | 2021 |
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Correction of X-Linked Severe Combined Immunodeficiency in Human Hematopoietic Stem and Progenitor Cells M Pavel-Dinu, VA Wiebking, N Gomez-Ospina, RO Bak, BT Dejene, ... MOLECULAR THERAPY 25 (5), 345-346, 2017 | | 2017 |